@article{ronzitti:hal-01474146,
  TITLE = {{A translationally optimized AAV-UGT1A1 vector drives safe and long-lasting correction of Crigler-Najjar syndrome}},
  AUTHOR = {Ronzitti, Giuseppe and Bortolussi, Giulia and van Dijk, Remco and Collaud, Fanny and Charles, Severine and Leborgne, Christian and Vidal, Patrice and Martin, Samia and Gjata, Bernard and Sola, Marcelo Simon and van Wittenberghe, Laetitia and Vignaud, Alban and Veron, Philippe and Bosma, Piter J and Muro, Andres F and Mingozzi, Federico},
  URL = {https://hal.sorbonne-universite.fr/hal-01474146},
  JOURNAL = {{Molecular Therapy - Methods and Clinical Development}},
  PUBLISHER = {{Cell Press}},
  VOLUME = {3},
  YEAR = {2016},
  DOI = {10.1038/mtm.2016.49},
  PDF = {https://hal.sorbonne-universite.fr/hal-01474146v1/file/1-s2.0-S2329050117300219-main.pdf},
  HAL_ID = {hal-01474146},
  HAL_VERSION = {v1},
}