@article{collaud:hal-04324427, TITLE = {{Preclinical Development of an AAV8-hUGT1A1 Vector for the Treatment of Crigler-Najjar Syndrome}}, AUTHOR = {Collaud, Fanny and Bortolussi, Giulia and Guianvarc'h, Laurence and Aronson, Sem and Bordet, Thierry and Veron, Philippe and Charles, Severine and Vidal, Patrice and Sola, Marcelo Simon and Rundwasser, Stephanie and Dufour, Delphine and Lacoste, Florence and Luc, Cyril and Wittenberghe, Laetitia and Martin, Samia and Le Bec, Christine and Bosma, Piter and Muro, Andres and Ronzitti, Giuseppe and Hebben, Matthias and Mingozzi, Federico}, URL = {https://hal.science/hal-04324427}, JOURNAL = {{Molecular Therapy - Methods and Clinical Development}}, PUBLISHER = {{Cell Press}}, VOLUME = {12}, PAGES = {157-174}, YEAR = {2019}, MONTH = Mar, DOI = {10.1016/j.omtm.2018.12.011}, HAL_ID = {hal-04324427}, HAL_VERSION = {v1}, }